Targeted gene correction of FKRP by CRISPR/Cas9 restores functional glycosylation of α- dystroglycan in cortical neurons derived from human induced pluripotent stem cells
نویسندگان
چکیده
Centre for Genomics and Child Health, Blizard Institute, Barts and the London School of Medicine and Dentistry, Queen Mary University of London, 4 Newark Street, London E1 2AT, UK Stem Cell Laboratory, National Bowel Research Centre, Blizard Institute, Barts and the London School of Medicine and Dentistry, Queen Mary University of London, 2 Newark Street, London E1 2AT, UK Wellcome Trust Sanger Institute, Wellcome Trust Genome Campus, Hinxton, Cambridge CB10 1SA, UK UCL Great Ormond Street Institute of Child Health, 30 Guilford Street, London WC1N 1EH, UK Co-first author
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تاریخ انتشار 2017